Blocking p62-dependent SMN degradation ameliorates spinal muscular atrophy disease phenotypes
Publication information:
Rodriguez-Muela N, Parkhitko A, Grass T, Gibbs RM, Norabuena EM, Perrimon N, Singh R, Rubin LL. Blocking p62-dependent SMN degradation ameliorates spinal muscular atrophy disease phenotypes. The Journal of Clinical Investigation. 2018;128(7):3008–3023.